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Lumbar Puncture Delivery of AAV9 in Juvenile Rats for CNS Gene Therapy
March 29, 2024
通过腰椎池注射在幼年大鼠中鞘内载体给药
01:24 min
•
制备试剂以递送腺相关血清型 9 载体
00:39 min
•
在幼鼠中通过腰椎穿刺递送基因治疗载体
02:41 min
•
Anthony Donsante
,
Shauna A. Rasmussen
,
Judith L. Fridovich-Keil
1
Department of Neurosurgery, School of Medicine
,
Emory University
,
2
Department of Human Genetics, School of Medicine
,
Emory University
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描述了一种外科手术,用于向幼年大鼠的腰椎池进行注射。这种方法已被用于基因治疗载体的鞘内递送,但预计这种方法可用于多种疗法,包括细胞和药物。
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